There is super exciting news in the world of cystic fibrosis today! Kalydeco, which is the first drug to actually treat the cause of CF instead of just the symptoms got approved by the FDA! It is only effective for 4% of those who have CF, but it is definitely a huge step in the right direction. Can't wait to see what they come up with next, and I have high hopes that it will be for those of us with the most common gene mutation, delta F508. My hopes are high.
This is the article from the Cystic Fibrosis Foundation. FDA Approves Kalydeco (VX-770) — First Drug That Targets the Underlying Cause of CF - CFF
This is the article from the FDA.
This is the article from Vertex which is the company that created Kalydeco.
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